How we serve

Our three goals

  • Fundraise to accelerate research and therapeutic innovations

    We’re at a critical moment in time for gene therapy research, and we provide fundraising advocacy, monetary support, and patient access for our research heroes. Our first step - funding $100,000 in preclinical research to establish a RORA mouse colony with disease characteristics.

    A female scientist in a white lab coat looking through a microscope in a laboratory with various lab supplies on shelves behind her.

  • Aggregate patient data to better understand RORA's impact

    We are in the process of determining the best way to aggregate patient data in collaboration with potential partners. This decision will be informed by both the research and patient communities.

    Person using a laptop with analytics and graph data on the screen, a smartphone and glasses on a white table, and a ceiling vent in the background.

  • Connect RORA families and individuals around the world

    We host community forums to connect on the latest research initiatives, share our experiences with RORA caregiving and development, and unite around our common goals.

    A woman smiling and walking with two young boys on a paved path in a park surrounded by green trees and foliage during daytime.